THE SOCIETY FOR INHERITED METABOLIC DISORDERS
Statement On Collaborative Outcomes Data
27 March, 2007
Current developments in understanding of human metabolism and genetics are providing exciting therapeutic options for treatment of inherited metabolic disorders. At the same time, we increasingly appreciate the complexity and variable expression of inherited metabolic disorders. Therefore, the SIMD membership strongly recommends that therapies introduced for clinical use should be implemented in the context of ongoing collaborative efforts toward collection of objective outcomes data.